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GM1 gangliosidosis is one of those diagnoses that can turn a family’s world upside down in a single appointment. One moment you’re searching for answers to unexplained symptoms, and the next, you’re learning about a fatal rare genetic condition most people have never even heard of.

Currently, there is no approved treatment or cure that stops or reverses the disease. However, we are in a “pivotal era” of research. Today, treatment means a dual approach: Expert Symptom Management and Investigational Research.

We are honored to share that our very own “Sweet Iris” and the mission of the Cure GM1 Foundation were recently featured in a moving segment on KRON 4 News. As we observe Rare Disease Day, this coverage shines a vital spotlight on the realities of living with GM1 Gangliosidosis and the urgent need for continued research and funding.

What Is GM1 Gangliosidosis? GM1 Gangliosidosis is a rare, inherited genetic disorder that affects the…