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CureGM1

Research

Enzyme Replacement Therapy Project

Enzyme Replacement Therapy Project

Read More Enzyme Replacement Therapy ProjectContinue

ERT Brochure

ERT Brochure

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Cure GM1 Invests $400,000 to Advance Development of Enzyme Replacement Therapy

January 26, 2025January 27, 2025

Cure GM1 is dedicated to investing in research, seeding new projects, and to the development…

Read More Cure GM1 Invests $400,000 to Advance Development of Enzyme Replacement TherapyContinue

2024 Cure GM1 Impact Report

January 1, 2025January 2, 2025

Our summary of impact in 2024 is now available to read. Although this year was hard with…

Read More 2024 Cure GM1 Impact ReportContinue

Sanofi Press Release: AMETHIST Trial Discontinued

April 25, 2024April 25, 2024

We regret to inform you that in Sanofi’s quarterly press release issued today that the…

Read More Sanofi Press Release: AMETHIST Trial DiscontinuedContinue

2023 Cure GM1 Impact Report – Annual Update And Beyond

February 18, 2024January 1, 2025

Our summary of impact in 2023 is now available to read. After some time reflecting, everyone…

Read More 2023 Cure GM1 Impact Report – Annual Update And BeyondContinue

Cure GM1 to Collaborate with xCURES for Natural History Study Pilot

December 6, 2023July 1, 2024

Cure GM1, a 501(c)(3) nonprofit organization located in Albany, CA, USA is proud to announce…

Read More Cure GM1 to Collaborate with xCURES for Natural History Study PilotContinue

Over $461K Grant toward Enzyme Replacement Therapy with TEGA Therapeutics

October 24, 2023November 27, 2023

TEGA Therapeutics, Inc. has been awarded a Phase I Small Business and Innovative Research (SBIR)…

Read More Over $461K Grant toward Enzyme Replacement Therapy with TEGA TherapeuticsContinue

Gelb Laboratory Publishes Third GM1 Newborn Screening Paper

July 7, 2023November 29, 2023

Cure GM1 provided seed funding for, and families from the GM1 community provided dried blood…

Read More Gelb Laboratory Publishes Third GM1 Newborn Screening PaperContinue

2022 Cure GM1 Impact Report – Impact in 2022 and Beyond

March 30, 2023November 14, 2023

Our summary of impact in 2022 is now available to read. After some time reflecting,…

Read More 2022 Cure GM1 Impact Report – Impact in 2022 and BeyondContinue

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501(c)(3) EIN: #47-3154419

PO Box 6890, Albany
CA 94706, USA
1-510-306-2460

Cure GM1 does not prescribe medications or treatments.  This information is being shared for educational purposes and discussion with your doctors.

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  • About GM1 Gangliosidosis
    • About
      • About GM1
      • Disease Overview PDF
      • Clinical Disease Overview Video
      • The Cause
      • Who Gets GM1
      • Incidence of GM1
      • History of GM1
      • Life Expectancy
      • Subtypes of GM1
    • Treatments and Research
      • Advancements and Research
    • If Your Loved One Has GM1
      • Join a Natural History Study
      • Give Samples to the GM1 Biobank
      • Participate in Data Sharing
      • Contact Us
  • How to Help
    • Take Action
    • By Donating
      • Donate
      • Paypal Giving Fund
      • Crypto
      • Contact Us
    • Read and Share Our Stories
      • Community Stories
      • Watch Family Videos
      • Share Your Story
    • For Researchers
      • Grants Overhead Policy
    • By Fundraising
      • Fundraise for CureGM1
      • Use Our Fundraising Manual
      • Fundraise with Charity Miles App
      • See Our Fundraising Ideas
      • Used Car Donation
      • GoFundMe
      • JustGiving
      • Facebook
    • Participate in Our Events
      • Rare Disease Day
      • GM1 Gangliosidosis Awareness Day
      • Move for GM1
      • Annual Conference
    • By Shopping
      • GM1 Store
      • RaiseRight
      • Buy Chocolate
      • eBay
    • Engage with Cure GM1
      • Contact Us
      • Subscribe to the Newsletter
      • Join the Cure GM1 Parents Facebook Group
      • Join the Friends of Cure GM1 Facebook Group
    • Subscribe to Our YouTube Channel
  • What We Do
    • About the Foundation
      • Mission Statement
      • Board Members and Staff
      • Scientific and Business Advisors
      • Informational Flyer
    • Newsletters
      • View Newsletters
      • Subscribe to the Newsletter
    • Advancements / Research
      • Enzyme Replacement Therapy Project
    • Guide Families
      • Message to the Newly Diagnosed
      • Learn about Data Sharing
      • Contact Us / Have questions?
    • Drive Progress and Research
      • FDA Engagement, EL-PFDD
      • Voice of the Patient Report
      • Caregiver Preferences Study