About CureGM1

The CURE GM1 FOUNDATION’s mission is to fund research for the benefit of all those who suffer from GM1 gangliosidosis.  This nonprofit organization was founded by parents of children who suffer from GM1 who seek to save the lives of all those who suffer from this wretched condition. The Cure GM1 Foundation is dedicated to directly funding research for a cure for GM1 gangliosidosis – a lysosomal storage disease that attacks the brain and spinal cord.  Over 50% of those impacted die before their fifth birthday.  GM1 is a progressive and degenerative condition with an extremely broad and debilitating array of symptoms and complications.

CURE GM1 is the only 501(c)(3) nonprofit entirely dedicated to GM1 Gangliosidosis research and drug development.  We have held GM1 research symposiums and GM1 community and family conferences.  Our meetings are attended by families from around the globe and help build momentum, community and progress.  Please see the Advancements/Research items for more information with respect to the overall research landscape and also projects we supported/initiated.

You can read more about us in our shareable Cure GM1 Foundation PDF.

The Internal Revenue Service approved the foundation’s 501(c)(3) status on April 15th, 2015. With the generous support of GM1 families, those affected by GM1, and the support of the world, we believe a cure can be found. We must contribute in any way possible to bring these treatments forward.  Every second that goes by, the world could be closer to an end to GM1 and an end to conditions like it, and innocent children who have the incredible misfortune of receiving disease-causing genes can finally have a chance at life.

Legal Representation

  • Hogan Lovells US LLP
  • Faber Daeufer & Itrato PC