2016 Cyclodextrin GM1 Pilot Study
GM1 Cyclodextrin Pilot Study Initiated This experiment was ceased due to lack of efficacy.
-
-
2015-2017 Auburn/UMass Research Intravenous AAV9 Gene Therapy
Cure GM1 funded pre-clinical studies, IND-enabling studies, and the Pre-IND briefing document for intravenous AAV9…
-
Syner-G Clinical Study
This clinical study was being conducted at University of Minnesota where the ketogenic diet was…
-
Althea’s Story
Althea was born on 23rd September 2016, a beautiful 6lb 8oz baby girl. Thea was…
-
-
Sage’s Story
Sage was born on November 20th, 2014, he was a 7 pound 15 ounce 20…
-
Aiden’s Story
Sweet Boy Aiden Aiden is 5 years old now. Things started off great then at…
-
Paola’s Story
Una Bellisima Bambina Paola is a beautiful child born on June 29, 2013. She was…
-
Joe’s Story
A special boy that fought to the end Joe was born 4 weeks early by…