Carter Michael’s Story
Carter’s story, by his mother “Carter Michael was diagnosed with GM1. He was our precious…
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Gael’s Story
Gael’s story, by his mother “Gael was diagnosed with Type 1 infantile GM1 on his…
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February 2025 Cure GM1 Catalyst
This month is all about love, awareness, and action as we celebrate Valentine’s Day and Rare Disease Month. We are also celebrating our founder Christine’s daughter’s 17th birthday. For all families with children impacted by GM1, each birthday is a celebration, but the passage of time and the progression of the disease marks these milestones.
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GM1 Research: Cure GM1 Invests $400,000 to Advance Development of Enzyme Replacement Therapy
Cure GM1 is dedicated to investing in research, seeding new projects, and to the development of multiple treatment modalities for GM1 gangliosidosis. In collaboration with our advisors and consultants, who have decades of experience in biotech and research, Cure GM1 has selected a contract research organization (CRO) to further the development of enzyme replacement therapy (ERT).
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Milah’s Story
Milah’s story, by her mother “Milah was diagnosed with GM1 Type 1 at 8 months…
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January 2025 Cure GM1 Catalyst
Thank you for an amazing year in 2024!
The impact of your support gives hope to children, brings comfort to families, and accelerates the research that could change lives. Your support means that not a single moment will be lost in our pursuit of better treatments and support for families affected by GM1. -
2024 Cure GM1 Impact Report
Our summary of impact in 2024 is now available to read. Although this year was hard with…
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Ben’s Story
Ben’s story, by his mother “Ben was diagnosed with juvenile GM1 on December 22, 2023,…
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Joaquim and Sofia’s Story
Joaquim and Sofia’s story, by their father “Our current focus is on keeping Joaquim as…
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Lucas’s Story
Lucas’s story, by his mother “Because of GM1, Lucas has not been able to grow…