What would it take for artificial intelligence to genuinely support people living with GM1 gangliosidosis? A 2026 Cure GM1 Community Conference presentation explored the need for context, safety, consent, privacy, and lived experience.
Cure GM1 Catalyst | November 2026 COMMUNITYADVOCACY CORNERGET INVOLVEDSHOP FOR GOOD This year, Iris turned…
Family stories, research updates and practical advice from the 2026 International GM1 Virtual Community Conference, held online on October 2, 2026.
September’s Do It for GM1 raised $34,804.78, conference highlights, Milo’s story, the Basion partnership, a UCSF prenatal gene therapy survey, and year-end plans.
Understanding your genetics report, and how the GLB1 gene links GM1 gangliosidosis and Morquio B,…
Fall is already here and this month, is your chance to participate in our Do It For GM1 campaign. And we have only one month to go before our virtual community conference! We just published the full agenda and the speaker bios. Check it out and register now.
A plain-language guide for families comparing AAV gene therapy and ex vivo lentiviral gene therapy for GM1 gangliosidosis, plus what recent research adds.
Milo’s Story Milo passed away from infantile GM1 (Type 1) on July 20, 2026. Below,…
Ayesha’s Story Ayesha is the only child of a family who has already endured heartbreaking…