GM1 Gangliosidosis vs. GM2 Gangliosidosis (Tay-Sachs / Sandhoff): Understanding the Differences
From First Clinical Descriptions to Modern Therapeutics, a plain-language guide for families and caregivers Why…
From First Clinical Descriptions to Modern Therapeutics, a plain-language guide for families and caregivers Why…
GM1 gangliosidosis is a rare, inherited disease that robs children of their abilities, and their…
Cure GM1 is dedicated to investing in research and to the development of multiple treatment…
Kinley and Kennedy’s story, by their father “The girls recently hit their 5-year post Gene…
This month as we give thanks, we want to express our deepest gratitude to this strong and resilient community. We’re thankful for all the truly kind support and generosity that fuels the work we do. While we truly wish that no one had to suffer from GM1 gangliosidosis.
Eva and Franco’s story, by their mother “We keep fighting for them and enjoying our…
Let’s take a minute to celebrate Christine, Connie, Niclas, and Kevin for “Doing It for GM1.” Their combined efforts have raised over $35K! The month closed with great news from SylamoreBio, who received a $3 million NIH grant to advance their innovative GM1 research.
Nella’s story, by her father “Nella is living with GM1 — she’s not defined by…
Aidan’s story, by his grandmother “Don’t give up hope, but cherish each moment.“ How did…