2023 Cure GM1 Impact Report – Annual Update And Beyond
Our summary of impact in 2023 is now available to read. After some time reflecting, everyone…
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Iris’ Story from Her Brother’s Perspective
As told by Iris’ brother. How has GM1 gangliosidosis affected your life? GM1 gangliosidosis is…
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Marley’s Story
How did you feel when your child received a diagnosis of GM1? Early on we…
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Jessica’s Story
How did you feel when you received a diagnosis of GM1? When I got my…
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Violet’s Story
The Law Family announces with the sweetest sorrow, the passing of their beloved daughter, Violet…
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Cure GM1 to Collaborate with xCURES for Natural History Study Pilot
Update (October 2026): This pilot has ended. Medical records from 4 patients were collected through…
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Over $461K Grant toward Enzyme Replacement Therapy with TEGA Therapeutics
Update (October 2026): Cure GM1’s collaboration with TEGA Therapeutics has ended, and the Cure GM1…
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Gelb Laboratory Publishes Third GM1 Newborn Screening Paper
Cure GM1 provided seed funding for, and families from the GM1 community provided dried blood…
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Asia’s Story
This is the story of Asia, a little princess born on December 6, 2020. Asia…