Hello! We have some incredible news for the GM1 community. In July, members of the Cure GM1 team met with representatives of the U.S. Food & Drug Administration (FDA) to discuss the future of Enzyme Replacement Therapy (ERT) as a treatment for those living with GM1 gangliosidosis.
Summer has a way of slowing things down, and we hope you are finding joy in relaxed routines, longer days, and more time with your precious families. I’m pleased to introduce our coordinator for this year’s virtual International Cure GM1 Community Conference, Cleopatra Frazier. She’ll be here to answer all of your questions and help us create an impactful and meaningful experience for all of you Oct. 2. More about Cleopatra below.
Happy June! This is our favorite month because it means International GM1 Gangliosidosis Awareness Day 2026 is almost here. Our June 2026 Cure GM1 Catalyst newsletter covers GM1 Awareness Day results, community stories, the latest research, and ways to get involved.
Happy May!
This is our favorite month because it means International GM1 Gangliosidosis Awareness Day 2026 is almost here!
For us, May 23 isn’t just a date on the calendar. It’s a powerful opportunity to honor the journeys of those impacted by GM1 and shine a powerful light on its impact on our global community.
As the year comes to an end, we remain focused on creating connection by keeping our rare disease community informed of advocacy opportunities, research news and community updates. Join us in learning more about our efforts to push for a cure for GM1 gangliosidosis.
As the year comes to an end, we remain focused on creating connection by keeping our rare disease community informed of advocacy opportunities, research news and community updates. Join us in learning more about our efforts to push for a cure for GM1 gangliosidosis.
As the year comes to an end, we remain focused on creating connection by keeping our rare disease community informed of advocacy opportunities, research news and community updates. Join us in learning more about our efforts to push for a cure for GM1 gangliosidosis.
2025 Cure GM1 Impact Report Check out what you helped us accomplish in 2025 All…
As the year comes to an end, we remain focused on creating connection by keeping our rare disease community informed of advocacy opportunities, research news and community updates. Join us in learning more about our efforts to push for a cure for GM1 gangliosidosis.