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About GM1 Gangliosidosis
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Research
Cure GM1 Foundation and TEGA Therapeutics Establish Collaboration to Develop GM1 Gangliosidosis Therapy
By
Rajiv Raman
August 24, 2021
November 27, 2023
TEGA Cure GM1 Collaboration PDF
TEGA WORLD Pres 2023
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Two New AAV Gene Therapy Clinical Trials for Infantile and Late Infantile GM1 to Begin in Q1/Q2 2021
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About GM1 Gangliosidosis
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About
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About GM1
Disease Overview PDF
Clinical Disease Overview Video
The Cause
Who Gets GM1
Incidence of GM1
History of GM1
Life Expectancy
Subtypes of GM1
Treatments and Research
Toggle child menu
Expand
Advancements and Research
If Your Loved One Has GM1
Toggle child menu
Expand
Participate in Research and Data Sharing
Join the GM1 Census
Join a Natural History Study
Give Samples to the GM1 Biobank
Contact Us
How to Help
Toggle child menu
Expand
Take Action
Toggle child menu
Expand
Join the GM1 Census
By Donating
Toggle child menu
Expand
Donate
Paypal Giving Fund
Crypto
Contact Us
Read and Share Our Stories
Toggle child menu
Expand
Community Stories
Watch Family Videos
Share Your Story
For Researchers
Toggle child menu
Expand
Grants Overhead Policy
By Fundraising
Toggle child menu
Expand
Fundraise for CureGM1
Toggle child menu
Expand
See Our Fundraising Ideas
Use Our Fundraising Manual
GoFundMe
JustGiving
Facebook
Used Car Donation
Participate in Our Events
Toggle child menu
Expand
See Our Annual Events
GM1 Awareness Day
Do It for GM1
Rare Disease Day
Annual Conference
By Shopping
Toggle child menu
Expand
GM1 Store
RaiseRight
Walmart Spark Good
Buy Chocolate
eBay
Engage with Cure GM1
Toggle child menu
Expand
Contact Us
Subscribe to the Newsletter
Subscribe to Our YouTube Channel
Join the Cure GM1 Parents Facebook Group
Join the Friends of Cure GM1 Facebook Group
What We Do
Toggle child menu
Expand
About the Foundation
Toggle child menu
Expand
Mission Statement
Board Members and Staff
Scientific and Business Advisors
Informational Flyer
Newsletters
Toggle child menu
Expand
View Newsletters
Subscribe to the Newsletter
Advancements / Research
Toggle child menu
Expand
Enzyme Replacement Therapy Project
Guide Families
Toggle child menu
Expand
Resources For GM1 Families
Join the GM1 Census
Participate in Research and Data Sharing
Contact Us / Have Questions?
Drive Progress and Research
Toggle child menu
Expand
FDA Engagement, EL-PFDD
Voice of the Patient Report
Caregiver Preferences Study
