Cure GM1 Allocates Up to $1.4 Million to Advance Enzyme Replacement Therapy
Cure GM1 is dedicated to investing in research and to the development of multiple treatment…
-
-
Kinley and Kennedy’s Story
Kinley and Kennedy’s story, by their father “The girls recently hit their 5-year post Gene…
-
November 2025 Cure GM1 Catalyst
This month as we give thanks, we want to express our deepest gratitude to this strong and resilient community. We’re thankful for all the truly kind support and generosity that fuels the work we do. While we truly wish that no one had to suffer from GM1 gangliosidosis.
-
Eva & Franco’s Story
Eva and Franco’s story, by their mother “We keep fighting for them and enjoying our…
-
October 2025 Cure GM1 Catalyst
Let’s take a minute to celebrate Christine, Connie, Niclas, and Kevin for “Doing It for GM1.” Their combined efforts have raised over $35K! The month closed with great news from SylamoreBio, who received a $3 million NIH grant to advance their innovative GM1 research.
-
Nella’s Story
Nella’s story, by her father “Nella is living with GM1 — she’s not defined by…
-
Aidan’s Story
Aidan’s story, by his grandmother “Don’t give up hope, but cherish each moment.“ How did…
-
September 2025 Cure GM1 Catalyst
What an incredible month August was! Our 2025 International GM1 Community Conference brought together participants from around the world. We were excited to hear from Azafaros that the first trial participant was enrolled in Portugal. We witnessed the power of our shared hope, courage, and commitment.
-
Tiffany’s Story
Tiffany’s story by her mother, Ruth “Tiffany has made me a better person. In spite…