This month is all about love, awareness, and action as we celebrate Valentine’s Day and Rare Disease Month. We are also celebrating our founder Christine’s daughter’s 17th birthday. For all families with children impacted by GM1, each birthday is a celebration, but the passage of time and the progression of the disease marks these milestones.
Cure GM1 is dedicated to investing in research, seeding new projects, and to the development of multiple treatment modalities for GM1 gangliosidosis. In collaboration with our advisors and consultants, who have decades of experience in biotech and research, Cure GM1 has selected a contract research organization (CRO) to further the development of enzyme replacement therapy (ERT).
Thank you for an amazing year in 2024!
The impact of your support gives hope to children, brings comfort to families, and accelerates the research that could change lives. Your support means that not a single moment will be lost in our pursuit of better treatments and support for families affected by GM1.
Our summary of impact in 2024 is now available to read. Although this year was hard with…
Lingxi’s GM1 Story, as told by her father Her GM1 Story ” We have been…
Hampus, Julia, and Isabella’s Story Their GM1 Stories “It is heartbreaking not knowing what tomorrow…
PEYTON’S STORY My Story “It has completely changed our family. We are closer than ever…
LUKE & ISAIAH our Story “Luke and Isaiah faced this horrible disease together, dying just…
Our summary of impact in 2023 is now available to read. After some time reflecting, everyone…
As told by Iris’ brother. How has GM1 gangliosidosis affected your life? GM1 Gangliosidosis is…