Ravi’s Story
Ravi’s Story Ravi passed away from infantile GM1 (Type 1) on March 4, 2026. Below,…
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August 2026 Cure GM1 Catalyst
Hello! We have some incredible news for the GM1 community. In July, members of the Cure GM1 team met with representatives of the U.S. Food & Drug Administration (FDA) to discuss the future of Enzyme Replacement Therapy (ERT) as a treatment for those living with GM1 gangliosidosis.
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GM1 Gangliosidosis vs. GM2 Gangliosidosis (Tay-Sachs / Sandhoff): Understanding the Differences
From First Clinical Descriptions to Modern Therapeutics, a plain-language guide for families and caregivers Why…
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How to Help Fund Research and Support the Cure GM1 Foundation
GM1 gangliosidosis is a rare, inherited disease that robs children of their abilities, and their…
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Cure GM1 Held an INTERACT Meeting About ERT with The FDA
Cure GM1 Moves ERT One Step Closer to A Trial We have some incredible news…
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GM1 Gangliosidosis: A History
GM1 Gangliosidosis: A History From First Clinical Descriptions to Modern Therapeutics Last updated August 2026…
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July 2026 Cure GM1 Catalyst
Summer has a way of slowing things down, and we hope you are finding joy in relaxed routines, longer days, and more time with your precious families. I’m pleased to introduce our coordinator for this year’s virtual International Cure GM1 Community Conference, Cleopatra Frazier. She’ll be here to answer all of your questions and help us create an impactful and meaningful experience for all of you Oct. 2. More about Cleopatra below.
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June 2026 Cure GM1 Catalyst
Happy June! This is our favorite month because it means International GM1 Gangliosidosis Awareness Day 2026 is almost here. Our June 2026 Cure GM1 Catalyst newsletter covers GM1 Awareness Day results, community stories, the latest research, and ways to get involved.
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Cure GM1 Allocates Up to $1.4 Million to Advance Enzyme Replacement Therapy
Cure GM1 is dedicated to investing in research and to the development of multiple treatment…