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Home / Blog - Page 10

Blog

Will Donation Ever Rule the World?

July 15, 2021October 19, 2023

Sed arcu non odio euismod lacinia. Sit amet cursus sit amet dictum sit. Nunc pulvinar…

Read More Will Donation Ever Rule the World?Continue

Emily’s Story

February 22, 2021January 25, 2024

Like most people, Emily Blu loves spending time with her friends, family, and online. She…

Read More Emily’s StoryContinue

Two New AAV Gene Therapy Clinical Trials for Infantile and Late Infantile GM1 to Begin in Q1/Q2 2021

January 11, 2021November 26, 2023

Cure GM1 is pleased to share the tremendous news that both  Passage Bio and Lysogene have received regulatory approvals…

Read More Two New AAV Gene Therapy Clinical Trials for Infantile and Late Infantile GM1 to Begin in Q1/Q2 2021Continue

Clara’s Story

December 1, 2020November 14, 2023

Please watch Clara’s family’s video: This is a wonderful article about Clara and her family’s…

Read More Clara’s StoryContinue

Cas’ Story

November 23, 2020November 26, 2023

From Cas’ Mother: Cas was a beautiful, happy boy.  He had beautiful eyes and hair…

Read More Cas’ StoryContinue

Sofia and Stephanie

August 25, 2020November 26, 2023

Sofia, developed up to 1 year and 8 months as a normal child, regression began…

Read More Sofia and StephanieContinue

Nastya’s Story

July 25, 2020November 26, 2023

Nastya’s Story Until the age of one year old, Nastya grew and developed like an…

Read More Nastya’s StoryContinue

Darian’s Story

July 1, 2020January 12, 2024

DONATE We are living a parents worst nightmare. Our sweet son Darian, was recently diagnosed…

Read More Darian’s StoryContinue

Conference Speakers

June 21, 2020November 14, 2023

Cure GM1 Conference Speakers Release Thank you for applying to be a speaker. First Name[text*…

Read More Conference SpeakersContinue

Elena’s Story

June 8, 2020November 14, 2023

Elena was diagnosed at age 23 and is from Russia.  She is the rare of…

Read More Elena’s StoryContinue

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  • About GM1 Gangliosidosis
    • About
      • About GM1
      • Disease Overview PDF
      • Clinical Disease Overview Video
      • The Cause
      • Who Gets GM1
      • Incidence of GM1
      • History of GM1
      • Life Expectancy
      • Subtypes of GM1
    • Treatments and Research
      • Advancements and Research
    • If Your Loved One Has GM1
      • Join a Natural History Study
      • Give Samples to the GM1 Biobank
      • Participate in Data Sharing
      • Contact Us
  • How to Help
    • Take Action
    • By Donating
      • Donate
      • Paypal Giving Fund
      • Crypto
      • Contact Us
    • Read and Share Our Stories
      • Community Stories
      • Watch Family Videos
      • Share Your Story
    • For Researchers
      • Grants Overhead Policy
    • By Fundraising
      • See Our Fundraising Ideas
      • Fundraise for CureGM1
        • Use Our Fundraising Manual
        • GoFundMe
        • JustGiving
        • Facebook
      • Used Car Donation
    • Participate in Our Events
      • GM1 Awareness Day
      • Do It for GM1
      • Rare Disease Day
      • Annual Conference
    • By Shopping
      • GM1 Store
      • RaiseRight
      • Buy Chocolate
      • eBay
    • Engage with Cure GM1
      • Contact Us
      • Subscribe to the Newsletter
      • Join the Cure GM1 Parents Facebook Group
      • Join the Friends of Cure GM1 Facebook Group
    • Subscribe to Our YouTube Channel
  • What We Do
    • About the Foundation
      • Mission Statement
      • Board Members and Staff
      • Scientific and Business Advisors
      • Informational Flyer
    • Newsletters
      • View Newsletters
      • Subscribe to the Newsletter
    • Advancements / Research
      • Enzyme Replacement Therapy Project
    • Guide Families
      • Resources For GM1 Families
      • Learn About Data Sharing
      • Contact Us / Have Questions?
    • Drive Progress and Research
      • FDA Engagement, EL-PFDD
      • Voice of the Patient Report
      • Caregiver Preferences Study