Cure GM1 is dedicated to investing in research, seeding new projects, and to the development of multiple treatment modalities for GM1 gangliosidosis. In collaboration with our advisors and consultants, who have decades of experience in biotech and research, Cure GM1 has selected a contract research organization (CRO) to further the development of enzyme replacement therapy (ERT).
Milah’s story, by her mother “Milah was diagnosed with GM1 Type 1 at 8 months…
Thank you for an amazing year in 2024!
The impact of your support gives hope to children, brings comfort to families, and accelerates the research that could change lives. Your support means that not a single moment will be lost in our pursuit of better treatments and support for families affected by GM1.
Our summary of impact in 2024 is now available to read. Although this year was hard with…
Ben’s story, by his mother “Ben was diagnosed with juvenile GM1 on December 22, 2023,…
Joaquim and Sofia’s story, by their father “Our current focus is on keeping Joaquim as…
Lucas’s story, by his mother “Because of GM1, Lucas has not been able to grow…
Aidan’s story, by his mother “This is my son, Aidan, who was diagnosed with GM1…
Lingxi’s GM1 Story, as told by her father Her GM1 Story ” We have been…