October 2026 Cure GM1 Catalyst
September’s Do It for GM1 raised $34,804.78, conference highlights, Milo’s story, the Basion partnership, a UCSF prenatal gene therapy survey, and year-end plans.
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September 2026 Cure GM1 Catalyst
Fall is already here and this month, is your chance to participate in our Do It For GM1 campaign. And we have only one month to go before our virtual community conference! We just published the full agenda and the speaker bios. Check it out and register now.
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Milo’s Story
Milo’s Story Milo passed away from infantile GM1 (Type 1) on July 20, 2026. Below,…
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Ayesha’s Story
Ayesha’s Story Ayesha is the only child of a family who has already endured heartbreaking…
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Ravi’s Story
Ravi’s Story Ravi passed away from infantile GM1 (Type 1) on March 4, 2026. Below,…
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August 2026 Cure GM1 Catalyst
Hello! We have some incredible news for the GM1 community. In July, members of the Cure GM1 team met with representatives of the U.S. Food & Drug Administration (FDA) to discuss the future of Enzyme Replacement Therapy (ERT) as a treatment for those living with GM1 gangliosidosis.
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July 2026 Cure GM1 Catalyst
Summer has a way of slowing things down, and we hope you are finding joy in relaxed routines, longer days, and more time with your precious families. I’m pleased to introduce our coordinator for this year’s virtual International Cure GM1 Community Conference, Cleopatra Frazier. She’ll be here to answer all of your questions and help us create an impactful and meaningful experience for all of you Oct. 2. More about Cleopatra below.