Evan’s Story
Evan lives in Arizona and is the son of Brad and Marilee Diagnosis – GM1…
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IntraBio Inc
Update (October 2026): IntraBio’s drug levacetylleucine (AQNEURSA) is now FDA approved for Niemann-Pick disease type…
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Eli’s Story
Eli lives in Arizona and is the son of Brad & Marilee Leishman Diagnosis –…
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Autumn’s Story
In Loving Memory of Autumn – A Happy Baby through all of the trials Autumn…
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Lenka’s Story of Hope – Lenka i Dobra Spółka
Thousands and thousands of miles away in Poland, a beautiful, sweet girl named Lenka suffers…
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Ian’s Story and Mission for a Cure
Little Ian was just recently diagnosed this year with Type 1/infantile GM1. Ian is a…
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In Loving Memory, Paxton’s Smiles and Brave Fight
Paxton, a first and only child, was born a seemingly healthy baby boy on Feb….
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In Loving Memory of Zac Milo Horspool
Born: Sat., Oct. 13, 2012 Died: Sat., Apr. 18, 2015 A precious angel returned to live with…