2018 Jackson Laboratory – Publicly Available Mouse Models
Dr. Cat Lutz and Dr. Aamir Zuberi are scientists at The Jackson Laboratory. Dr. Lutz…
2017 Dorphan Small Molecule Research and Mouse Study
Cure GM1 granted funds for a drug repurposing project and mouse study to study a…
2017 UC Davis Lentiviral Gene Therapy Research
Cure GM1 recently granted funds towards the development of a lentiviral gene therapy approach using…
2016 Cyclodextrin GM1 Pilot Study
GM1 Cyclodextrin Pilot Study Initiated This experiment was ceased due to lack of efficacy.
2015-2017 Auburn/UMass Research Intravenous AAV9 Gene Therapy
Cure GM1 funded pre-clinical studies, IND-enabling studies, and the Pre-IND briefing document for intravenous AAV9…
Syner-G Clinical Study
This clinical study was being conducted at University of Minnesota where the ketogenic diet was…
Althea’s Story
Althea was born on 23rd September 2016, a beautiful 6lb 8oz baby girl. Thea was…
Paxton’s Story
A beautiful baby boy born February 16, 2012 Paxton is our first and only child,…
Kate’s Story #AWin4Kate
#AWin4Kate Kate was born May 17, 2011, a healthy and happy baby. We always thought…
Joe’s Story
A special boy that fought to the end Joe was born 4 weeks early by…