Stella and Finya
Beautiful Stella and Finya passed away within one day of one another. Finya passed…
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Tyson’s Story
Our dear little Tyson was born on September 15, 1989 and lived a short 16…
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James’ Story
From James’ Mother: James was diagnosed with GM1 Gangliosidosis Type 2 Juvenile on November 7,…
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Eve’s Story
From Eve’s Mother We live in Ukraine in the Odessa region. Eve was born…
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A Newborn Screening Assay for GM1 Gangliosidosis, Gelb Laboratory, University of Washington
Tandem Mass Spectrometry Assay of Beta-Galactosidase for Multiplex Newborn Screening of GM1 Gangliosidosis Michael H….
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Sing Me a Story
We are pleased to announce a special nonprofit partnership with the Sing Me a Story…
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Pia’s Story
From Pia’s Mother: Hello, my name is Stefany Sanchez. I am 23 years old. My…
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Fatima and Sultan
From Sultan and Fatima’s mother: I am Sultan Ali and Fatima Shoaib Ali’s mother. …
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Eva’s Story
Eva Maria 15.01.16-31.05.19
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First Gene Therapy Clinical Trial Initiated May 2019!
The first gene therapy clinical trial for GM1 Gangliosidosis is a beacon of hope for…