Signs of Hope
Where are you promoting GM1 awareness? Wherever your adventures take you, join our Signs of…
-
-
Cure GM1 Foundation and TEGA Therapeutics Establish Collaboration to Develop GM1 Gangliosidosis Therapy
Update (October 2026): Cure GM1’s collaboration with TEGA Therapeutics has ended, and the Cure GM1…
-
Emily’s Story
Like most people, Emily Blu loves spending time with her friends, family, and online. She…
-
Two New AAV Gene Therapy Clinical Trials for Infantile and Late Infantile GM1 to Begin in Q1/Q2 2021
Update (October 2026): Lysogene, Sio Gene Therapies (formerly Axovant) and Passage Bio no longer exist….
-
Clara’s Story
Please watch Clara’s family’s video: This is a wonderful article about Clara and her family’s…
-
Cas’ Story
From Cas’ Mother: Cas was a beautiful, happy boy. He had beautiful eyes and hair…
-
Sofia and Stephanie
Sofia, developed up to 1 year and 8 months as a normal child, regression began…
-
Nastya’s Story
Nastya’s Story Until the age of one year old, Nastya grew and developed like an…
-
Darian’s Story
DONATE We are living a parents worst nightmare. Our sweet son Darian, was recently diagnosed…